In vivo genome editing with a small Cas9 orthologue derived from Campylobacter jejuni
2017 · Nature Communications · 725 citations
https://doi.org/10.1038/ncomms14500
D
Dong Woo Song
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Dong Woo Song is an academic researcher. The author has contributed to research in topics: CRISPR and Genetic Engineering & RNA Interference and Gene Delivery & MicroRNA in disease regulation. The author has an h-index of 11, co-authored 21 publications.
ORCID: 0000-0001-9700-7759Papers by this author
worksIn vivo delivery of CRISPR-Cas9 using lipid nanoparticles enables antithrombin gene editing for sustainable hemophilia A and B therapy
2022 · Science Advances · 174 citations
https://doi.org/10.1126/sciadv.abj6901
CRISPR-Cas9–mediated therapeutic editing of <i>Rpe65</i> ameliorates the disease phenotypes in a mouse model of Leber congenital amaurosis
2019 · Science Advances · 100 citations
https://doi.org/10.1126/sciadv.aax1210
Genome editing-mediated knock-in of therapeutic genes ameliorates the disease phenotype in a model of hemophilia
2022 · Molecular Therapy — Nucleic Acids · 15 citations
https://doi.org/10.1016/j.omtn.2022.08.002
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