Nusinersen initiated in infants during the presymptomatic stage of spinal muscular atrophy: Interim efficacy and safety results from the Phase 2 NURTURE study
2019 · Neuromuscular Disorders · 612 citations
https://doi.org/10.1016/j.nmd.2019.09.007
V
Valeria Sansone
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Valeria Sansone is an academic researcher from University of Milan. The author has contributed to research in topics: Neurogenetic and Muscular Disorders Research & Genetic Neurodegenerative Diseases & Muscle Physiology and Disorders. The author has an h-index of 52, co-authored 323 publications.
ORCID: 0000-0002-1354-3800Papers by this author
worksMotor function in type 2 and 3 SMA patients treated with Nusinersen: a critical review and meta-analysis
2021 · Orphanet Journal of Rare Diseases · 177 citations
https://doi.org/10.1186/s13023-021-02065-z
Nusinersen in type 1 spinal muscular atrophy: Twelve‐month real‐world data
2019 · Annals of Neurology · 120 citations
https://doi.org/10.1002/ana.25533
Continued benefit of nusinersen initiated in the presymptomatic stage of spinal muscular atrophy: 5‐year update of the<scp>NURTURE</scp>study
2023 · Muscle & Nerve · 100 citations
https://doi.org/10.1002/mus.27853
Respiratory Trajectories in Type 2 and 3 Spinal Muscular Atrophy in the iSMAC Cohort Study
2020 · Neurology · 69 citations
https://doi.org/10.1212/wnl.0000000000011051
Measuring Outcomes in Adults with Spinal Muscular Atrophy – Challenges and Future Directions – Meeting Report
2020 · Journal of Neuromuscular Diseases · 63 citations
https://doi.org/10.3233/jnd-200534
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