Final results of the phase 1/2, open-label clinical study of intravenous recombinant human N-acetyl-α-d-glucosaminidase (SBC-103) in children with mucopolysaccharidosis IIIB
2018 · Molecular Genetics and Metabolism · 24 citations
https://doi.org/10.1016/j.ymgme.2018.12.003