Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response
2006 · Nature Medicine · 2,102 citations
https://doi.org/10.1038/nm1358
M
Margareth C. Ozelo
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Margareth C. Ozelo is an academic researcher from Universidade Estadual de Campinas (UNICAMP). The author has contributed to research in topics: Hemophilia Treatment and Research & Platelet Disorders and Treatments & Blood Coagulation and Thrombosis Mechanisms. The author has an h-index of 34, co-authored 193 publications.
ORCID: 0000-0001-5938-0675Papers by this author
worksASH ISTH NHF WFH 2021 guidelines on the management of von Willebrand disease
2021 · Blood Advances · 341 citations
https://doi.org/10.1182/bloodadvances.2020003264
Global Seroprevalence of Pre-existing Immunity Against AAV5 and Other AAV Serotypes in People with Hemophilia A
2022 · Human Gene Therapy · 98 citations
https://doi.org/10.1089/hum.2021.287
Gene Therapy with Fidanacogene Elaparvovec in Adults with Hemophilia B
2024 · New England Journal of Medicine · 66 citations
https://doi.org/10.1056/nejmoa2302982
Evaluation of the immature platelet fraction contribute to the differential diagnosis of hereditary, immune and other acquired thrombocytopenias
2017 · Scientific Reports · 52 citations
https://doi.org/10.1038/s41598-017-03668-y
Safety and efficacy of long‐term emicizumab prophylaxis in hemophilia A with factor VIII inhibitors: A phase 3b, multicenter, single‐arm study (STASEY)
2022 · Research and Practice in Thrombosis and Haemostasis · 48 citations
https://doi.org/10.1002/rth2.12837
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